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Trial details imported from ClinicalTrials.gov

For full trial details, please see the original record at https://clinicaltrials.gov/study/NCT01072175




Registration number
NCT01072175
Ethics application status
Date submitted
12/02/2010
Date registered
19/02/2010

Titles & IDs
Public title
Investigate Safety, Pharmacokinetics and Pharmacodynamics of GSK2118436 & GSK1120212
Scientific title
An Open-Label, Dose-Escalation, Phase I/II Study to Investigate the Safety, Pharmacokinetics, Pharmacodynamics and Clinical Activity of the BRAF Inhibitor GSK2118436 in Combination With the MEK Inhibitor GSK1120212 in Subjects With BRAF Mutant Metastatic Melanoma
Secondary ID [1] 0 0
113220
Universal Trial Number (UTN)
Trial acronym
Linked study record

Health condition
Health condition(s) or problem(s) studied:
Cancer 0 0
Condition category
Condition code

Intervention/exposure
Study type
Interventional
Description of intervention(s) / exposure
Treatment: Drugs - GSK2118436
Treatment: Drugs - GSK1120212

Experimental: Arm Part A - Day 1: GSK2118436 75mg; Day 2 through Day 16: GSK1120212 2mg; Day 15: GSK2118436 75mg +GSK1120212 2mg Drug-drug interaction

Experimental: Arm Part B - GSK2118436 + GSK1120212 Dose escalation to a maximum tolerated combination dose

Experimental: Arm Part C - GSK2118436 + GSK1120212 cohort expansion for safety and efficacy


Treatment: Drugs: GSK2118436
GSK2118436 is a potent and selective inhibitor of BRAF kinase activity with a mode of action consistent with adenosine triphosphate-competitive inhibition.

Treatment: Drugs: GSK1120212
GSK1120212 is a potent and highly selective inhibitor of MEK1/2 activation and kinase activity.

Intervention code [1] 0 0
Treatment: Drugs
Comparator / control treatment
Control group

Outcomes
Primary outcome [1] 0 0
Part A: Maximum Plasma Concentration (Cmax) of a Single Dose of Dabrafenib Administered Alone and in Combination With Trametnib
Timepoint [1] 0 0
Day 15
Primary outcome [2] 0 0
Part A: AUC (0-t) and AUC (0-inf) of Dabrafenib and Its Metabolites
Timepoint [2] 0 0
Day 15
Primary outcome [3] 0 0
Part B: Number of Participants With Any Adverse Event (AE) or Serious Adverse Event (SAE)
Timepoint [3] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 8 years)
Primary outcome [4] 0 0
Part B: Number of Participants With Worst-case Chemistry Toxicity Grade Change From Baseline
Timepoint [4] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 8 years)
Primary outcome [5] 0 0
Part B: Number of Participants With Worst-case Chemistry Change From Baseline With Respect to Normal Range
Timepoint [5] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 8 years)
Primary outcome [6] 0 0
Part B: Number of Participants With Worst-case Hematology Toxicity Grade Change From Baseline
Timepoint [6] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 8 years)
Primary outcome [7] 0 0
Part B: Number of Participants With Worst-case Hematology Change From Baseline With Respect to Normal Range
Timepoint [7] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 8 years)
Primary outcome [8] 0 0
Part B: Number of Participants With the Indicated Worst-case Change From Baseline in Heart Rate and Blood Pressure
Timepoint [8] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 8 years)
Primary outcome [9] 0 0
Part C (Randomized): Number of Participants With BRAF Mutant Metastatic Melanoma With Best Overall Response as Assessed by the Investigator
Timepoint [9] 0 0
From the first dose of study medication to the first documented evidence of a confirmed complete response or partial response (up to approximately 7 years)
Primary outcome [10] 0 0
Part C (Randomized): Number of Participants With BRAF Mutant Metastatic Melanoma With Best Overall Response Assessed by Blinded Independent Central Review (BICR)
Timepoint [10] 0 0
From the first dose of study medication to the first documented evidence of a confirmed complete response or partial response (up to approximately 19 months)
Primary outcome [11] 0 0
Part C (Crossover): Number of Participants With BRAF Mutant Metastatic Melanoma With Best Overall Response as Assessed by the Investigator
Timepoint [11] 0 0
From the first dose of study medication to the first documented evidence of a confirmed complete response or partial response (up to approximately 7 years)
Primary outcome [12] 0 0
Part C (Randomized): Progression-free Survival (PFS) as Assessed by the Investigator
Timepoint [12] 0 0
From the date of randomization to the earliest date of disease progression (PD) or death due to any cause (up to approximately 7 years)
Primary outcome [13] 0 0
Part C (Crossover): Progression-free Survival (PFS) as Assessed by the Investigator
Timepoint [13] 0 0
From the first dose of study medication to the earliest date of disease progression (PD) or death due to any cause (up to approximately 7 years)
Primary outcome [14] 0 0
Part C (Randomized): Progression-free Survival (PFS) as Assessed by the Blinded Independent Central Review (BICR)
Timepoint [14] 0 0
From the date of randomization to the earliest date of disease progression (PD) or death due to any cause (up to approximately 19 months)
Primary outcome [15] 0 0
Part C (Randomized): Duration of Response as Assessed by the Investigator and Blinded Independent Central Review (BICR)
Timepoint [15] 0 0
First documented evidence of PR or CR until the date of the first documented sign of disease progression or the date of death due to any cause (up to approximately 19 months)
Primary outcome [16] 0 0
Part C (Randomized): Number of Participants With Any Adverse Event (AE) or Serious Adverse Event (SAE)
Timepoint [16] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 7 years)
Primary outcome [17] 0 0
Part C (Randomized): Number of Participants With Worst-case Chemistry Toxicity Grade Change From Baseline
Timepoint [17] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 7 years)
Primary outcome [18] 0 0
Part C (Randomized): Number of Participants With Worst-case Chemistry Change From Baseline With Respect to Normal Range
Timepoint [18] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 7 years)
Primary outcome [19] 0 0
Part C (Randomized): Number of Participants With Worst-case Hematology Toxicity Grade Change From Baseline
Timepoint [19] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 7 years)
Primary outcome [20] 0 0
Part C (Randomized): Number of Participants With Worst-case Hematology Change From Baseline With Respect to Normal Range
Timepoint [20] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 7 years)
Primary outcome [21] 0 0
Part C (Randomized): Number of Participants With the Indicated Worst-case Change From Baseline in Heart Rate and Blood Pressure
Timepoint [21] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 7 years)
Primary outcome [22] 0 0
Part D (Analyte=GSK2118436): Maximum Plasma Concentration (Cmax) of a Single and Repeat Dose of Dabrafenib Alone and in Combination With Trametinib
Timepoint [22] 0 0
Day 1 and Day 21
Primary outcome [23] 0 0
Part D (Analyte=GSK2118436): Tmax of a Single and Repeat Dose of Dabrafenib Alone and in Combination With Trametinib
Timepoint [23] 0 0
Day 1 and Day 21
Primary outcome [24] 0 0
Part D (Analyte=GSK2118436): AUC (0-tau) and AUC (0-inf) of Single and Repeat Doses of Dabrafenib Alone and in Combination With Trametinib
Timepoint [24] 0 0
Day 1 and Day 21
Primary outcome [25] 0 0
Part D: Number of Participants With Any Adverse Event (AE) or Serious Adverse Event (SAE)
Timepoint [25] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 7 years)
Primary outcome [26] 0 0
Part D: Number of Participants With Worst-case Chemistry Toxicity Grade Change From Baseline
Timepoint [26] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 7 years)
Primary outcome [27] 0 0
Part D: Number of Participants With Worst-case Chemistry Change From Baseline With Respect to Normal Range
Timepoint [27] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 7 years)
Primary outcome [28] 0 0
Part D: Number of Participants With Worst-case Hematology Toxicity Grade Change From Baseline
Timepoint [28] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 7 years)
Primary outcome [29] 0 0
Part D: Number of Participants With Worst-case Hematology Change From Baseline With Respect to Normal Range
Timepoint [29] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 7 years)
Primary outcome [30] 0 0
Part D: Number of Participants With the Indicated Worst-case Change From Baseline in Heart Rate and Blood Pressure
Timepoint [30] 0 0
From Baseline (Day 1) until Follow-up visit (up to approximately 7 years)
Secondary outcome [1] 0 0
Part A: Steady State Concentration of Trametinib With Concomitant Administration of Dabrafenib
Timepoint [1] 0 0
Day 15 and Day 16
Secondary outcome [2] 0 0
Part B: AUC [0-tau] of Dabrafenib (DAB) and Its Metabolite in Combination With Trametinib
Timepoint [2] 0 0
Day 15 and Day 21
Secondary outcome [3] 0 0
Part B: Pre-dose (Trough) Concentration at the End of the Dosing Interval (Ctau) and Maximum Plasma Concentration (Cmax) of Dabrafenib and Its Metabolite in Combination With Trametinib
Timepoint [3] 0 0
Day 15 and Day 21
Secondary outcome [4] 0 0
Part B: Tmax of Dabrafenib and Its Metabolite in Combination With Trametinib
Timepoint [4] 0 0
Day 15 and Day 21
Secondary outcome [5] 0 0
Part B (Analyte=GSK1120212): AUC (0-tau) Assessment of Trametinib in Combination With Dabrafenib
Timepoint [5] 0 0
Day 15 and Day 21
Secondary outcome [6] 0 0
Part B (Analyte=GSK1120212): Ctau and Cmax Assessments of Trametinib in Combination With Dabrafenib
Timepoint [6] 0 0
Day 15 and Day 21
Secondary outcome [7] 0 0
Part B (Analyte=GSK1120212): Tmax Assessment of Trametinib in Combination With Dabrafenib
Timepoint [7] 0 0
Day 15 and Day 21
Secondary outcome [8] 0 0
Part B: Number of Participants With BRAFi-naïve Mutant Metastatic Melanoma With the Best Overall Response as Assessed by Investigator
Timepoint [8] 0 0
From the first dose of study medication to the first documented evidence of a confirmed complete response or partial response (up to approximately 8 years)
Secondary outcome [9] 0 0
Part B: Duration of Response as Assessed by the Investigator in Participants With BRAFi-naïve Mutant Metastatic Melanoma
Timepoint [9] 0 0
First documented evidence of PR or CR until the earlier of date of disease progression or date of death due to any cause (up to approximately 8 years)
Secondary outcome [10] 0 0
Part B: Progression-free Survival (PFS) as Assessed by the Investigator in Participants With BRAFi-naïve Mutant Metastatic Melanoma
Timepoint [10] 0 0
From the date of first dose to the earliest date of disease progression (PD) or death due to any cause (up to approximately 8 years)
Secondary outcome [11] 0 0
Part B: Overall Survival (OS) in BRAFi Naïve Melanoma Participants
Timepoint [11] 0 0
From the date of first dose until date of death due to any cause (up to approximately 8 years)
Secondary outcome [12] 0 0
Part B: Pre- and Post-dose H-scores for Individual Participants
Timepoint [12] 0 0
Screening and at disease progression (up to approximately 8 years)
Secondary outcome [13] 0 0
Part C (Randomized): Overall Survival (OS)
Timepoint [13] 0 0
From the date of randomization until date of death due to any cause (up to approximately 7 years)
Secondary outcome [14] 0 0
Part C: Plasma Concentrations of Dabrafenib and Its Metabolites
Timepoint [14] 0 0
Day 15, Week 8, Week 16, Week 24, Week 32, Week 40, Week 48, and Week 56
Secondary outcome [15] 0 0
Part C: Plasma Concentrations of Trametinib
Timepoint [15] 0 0
Day 15, Week 8, Week 16, Week 24, Week 32, Week 40, Week 48, and Week 56
Secondary outcome [16] 0 0
Part C: Oral Clearance (CL/F) of Dabrafenib and Trametinib
Timepoint [16] 0 0
Day 15, Week 8, Week 16, Week 24, Week 32, Week 40, and Week 48
Secondary outcome [17] 0 0
Part C: Oral Volume of Distribution (V/F) of Dabrafenib and Trametinib
Timepoint [17] 0 0
Day 15, Week 8, Week 16, Week 24, Week 32, Week 40, and Week 48
Secondary outcome [18] 0 0
Part D: Cmax of Dabrafenib Metabolites
Timepoint [18] 0 0
Day 1: pre-dose, and 0.5, 1, 1.5, 2, 3, 4, 6, 8, 10, and 24 hours post dose. Day 21: pre-dose and 0.5, 1, 1.5, 2, 3, 4, 6, 8, and 10 hours post-dose
Secondary outcome [19] 0 0
Part D: Tmax of Dabrafenib Metabolites
Timepoint [19] 0 0
Day 1: pre-dose, and 0.5, 1, 1.5, 2, 3, 4, 6, 8, 10, and 24 hours post dose. Day 21: pre-dose and 0.5, 1, 1.5, 2, 3, 4, 6, 8, and 10 hours post-dose
Secondary outcome [20] 0 0
Part D: Area Under the Concentration-time Curve (AUC) of Dabrafenib Metabolites
Timepoint [20] 0 0
Day 1: pre-dose, and 0.5, 1, 1.5, 2, 3, 4, 6, 8, 10, and 24 hours post dose. Day 21: pre-dose and 0.5, 1, 1.5, 2, 3, 4, 6, 8, and 10 hours post-dose
Secondary outcome [21] 0 0
Part D: Cmax Assessment of Trametinib
Timepoint [21] 0 0
Day 1: pre-dose, and 0.5, 1, 1.5, 2, 3, 4, 6, 8, 10, and 24 hours post dose. Day 21: pre-dose and 0.5, 1, 1.5, 2, 3, 4, 6, 8, and 10 hours post-dose
Secondary outcome [22] 0 0
Part D: Tmax Assessment of Trametinib
Timepoint [22] 0 0
Day 1: pre-dose, and 0.5, 1, 1.5, 2, 3, 4, 6, 8, 10, and 24 hours post dose. Day 21: pre-dose and 0.5, 1, 1.5, 2, 3, 4, 6, 8, and 10 hours post-dose
Secondary outcome [23] 0 0
Part D: Area Under the Concentration-time Curve Assessment of Trametinib
Timepoint [23] 0 0
Day 1: pre-dose, and 0.5, 1, 1.5, 2, 3, 4, 6, 8, 10, and 24 hours post dose. Day 21: pre-dose and 0.5, 1, 1.5, 2, 3, 4, 6, 8, and 10 hours post-dose
Secondary outcome [24] 0 0
Part D: Number of Participants With the Best Overall Response as Assessed by the Investigator in Participants
Timepoint [24] 0 0
From the date of first dose of study medication to the first documented evidence of a confirmed complete response or partial response (up to approximately 7 years)
Secondary outcome [25] 0 0
Part D: Duration of Response as Assessed by the Investigator
Timepoint [25] 0 0
First documented evidence of PR or CR until the earlier of date of disease progression or date of death due to any cause (up to approximately 7 years)
Secondary outcome [26] 0 0
Part D: Progression-free Survival (PFS) as Assessed by the Investigator
Timepoint [26] 0 0
From the date of randomization to the earliest date of disease progression (PD) or death due to any cause (up to approximately 7 years)
Secondary outcome [27] 0 0
Part D: Overall Survival (OS)
Timepoint [27] 0 0
From the date of first dose until date of death due to any cause (up to approximately 7 years)

Eligibility
Key inclusion criteria
Key

* Capable of given written informed consent, which includes compliance with the requirements and restrictions listed in the consent form.
* Male or female age 18 years or greater; able to swallow and retain oral medication.
* BRAF mutation positive melanoma or colorectal cancer; other BRAF mutation positive tumor types may be considered.
* Measurable disease according to RECIST version 1.1.
* Eastern Cooperative Oncology Group Performance Status of 0 or 1 for Parts A and B. Subjects with Eastern Cooperative Oncology Group Performance Status of 2 or less may be entered into Part C with approval of medical monitor.
* Agree to contraception requirements.
* Calcium phosphorus product less than 4.0mmol2/L2.
* Adequate organ system function.

Key
Minimum age
18 Years
Maximum age
No limit
Sex
Both males and females
Can healthy volunteers participate?
No
Key exclusion criteria
* Currently receiving cancer therapy (chemotherapy, radiation therapy, immunotherapy, or biologic therapy).
* Part A and Part B: Prior exposure to BRAF or MEK inhibitors unless approved by the GSK Medical Monitor.
* Part C: Prior exposure to BRAF or MEK inhibitors. Prior anti-cancer therapy in the metastatic setting, with the exception of up to one regimen of chemotherapy and/or interleukin-2 (IL-2).
* Part D: Prior exposure to BRAF inhibitors. A washout period of 6 weeks is required for ipilimumab.
* Received an investigational anti-cancer drug within 4 weeks or 5 half-lives (whichever is shorter) of study drug administration--- at least 14 days must have passed between the last dose of prior investigational anti-cancer drug and the first dose of study drug.
* Current use of a prohibited medication or requires any of these medications during treatment with study drug.
* Current use of therapeutic warfarin.
* Any major surgery, radiotherapy, or immunotherapy within the last 4 weeks. Limited radiotherapy within the last 2 weeks.
* Chemotherapy regimens with delayed toxicity within the last 4 weeks. Chemotherapy regimens given continuously or on a weekly basis with limited potential for delayed toxicity within the last 2 weeks.
* Unresolved toxicity greater than National Cancer Institute-Common Terminology Criteria for Adverse Events version 4 Grade 1 from previous anti-cancer therapy except alopecia.
* History of retinal vein occlusion, central serous retinopathy or glaucoma.
* Predisposing factors to retinal vein occlusion including uncontrolled hypertension, uncontrolled diabetes, uncontrolled hyperlipidemia, and coagulopathy.
* Visible retinal pathology as assessed by ophthalmologic exam that is considered a risk factor for retinal vein occlusion or central serous retinopathy.
* Intraocular pressure greater than 21mm Hg as measured by tonography.
* Glaucoma diagnosed within one month prior to study Day 1.
* Presence of active gastrointestinal disease or other condition that will interfere significantly with the absorption, distribution, metabolism or excretion of drugs.
* Known human immunodeficiency virus, Hepatitis B or Hepatitis C infection.
* Primary malignancy of the central nervous system.
* Untreated or symptomatic brain metastasis, leptomeningeal disease or spinal cord compression. Subjects who are on a stable dose of corticosteroids for more than 1 month or off corticosteroids for 2 weeks can be enrolled with approval of medical monitor. Subjects are not permitted to receive enzyme-inducing anti-epileptic drugs.
* Subjects with brain metastases are excluded, unless

a. All known lesions must be previously treated with surgery or stereotactic radiosurgery, and- b. Brain lesion(s), if still present, must be confirmed stable (i.e. no increase in lesion size) for =90 days prior to first dose on study (must be documented with two consecutive MRI or CT scans using contrast), and c. Asymptomatic with no corticosteroids requirement for = 30 days prior to first dose on study, and d. No enzyme-inducing anticonvulsants for = 30 days prior to first dose on study.
* History of alcohol or drug abuse within 6 months prior to screening.
* Psychological, familial, sociological or geographical conditions that do not permit compliance with the protocol.
* QTc interval greater than or equal to 480msecs.
* History of acute coronary syndromes (including unstable angina), coronary angioplasty, or stenting within the past 24 weeks.
* Class II, III, or IV heart failure as defined by the New York Heart Association functional classification system.
* Abnormal cardiac valve morphology (subjects with minimal abnormalities can be entered on study with approval from the medical monitor.
* Treatment refractory hypertension defined as a blood pressure of systolic> 140 mmHg and/or diastolic > 90 mm Hg which cannot be controlled by anti-hypertensive therapy
* Patients with intra-cardiac defibrillators or permanent pacemakers.
* Cardiac metastases
* Known immediate or delayed hypersensitivity reaction or idiosyncrasy to drugs chemically related to the study drugs or excipients.
* Pregnant or lactating female.
* Unwillingness or inability to follow the procedures required in the protocol.
* Uncontrolled diabetes, hypertension or other medical conditions that may interfere with assessment of toxicity.
* Subjects with known glucose 6 phosphate dehydrogenase deficiency.

Study design
Purpose of the study
Treatment
Allocation to intervention
Non-randomised trial
Procedure for enrolling a subject and allocating the treatment (allocation concealment procedures)
Methods used to generate the sequence in which subjects will be randomised (sequence generation)
Masking / blinding
Open (masking not used)
Who is / are masked / blinded?



Intervention assignment
Other design features
Phase
Phase 2
Type of endpoint/s
Statistical methods / analysis

Recruitment
Recruitment status
Completed
Data analysis
Reason for early stopping/withdrawal
Other reasons
Date of first participant enrolment
Anticipated
Actual
Date of last participant enrolment
Anticipated
Actual
Date of last data collection
Anticipated
Actual
Sample size
Target
Accrual to date
Final
Recruitment in Australia
Recruitment state(s)
NSW,VIC
Recruitment hospital [1] 0 0
Novartis Investigative Site - Westmead
Recruitment hospital [2] 0 0
Novartis Investigative Site - Heidelberg
Recruitment postcode(s) [1] 0 0
2145 - Westmead
Recruitment postcode(s) [2] 0 0
3084 - Heidelberg
Recruitment outside Australia
Country [1] 0 0
United States of America
State/province [1] 0 0
California
Country [2] 0 0
United States of America
State/province [2] 0 0
Colorado
Country [3] 0 0
United States of America
State/province [3] 0 0
Connecticut
Country [4] 0 0
United States of America
State/province [4] 0 0
Florida
Country [5] 0 0
United States of America
State/province [5] 0 0
Maryland
Country [6] 0 0
United States of America
State/province [6] 0 0
Massachusetts
Country [7] 0 0
United States of America
State/province [7] 0 0
Minnesota
Country [8] 0 0
United States of America
State/province [8] 0 0
Pennsylvania
Country [9] 0 0
United States of America
State/province [9] 0 0
Tennessee
Country [10] 0 0
United States of America
State/province [10] 0 0
Texas

Funding & Sponsors
Primary sponsor type
Commercial sector/industry
Name
Novartis Pharmaceuticals
Address
Country

Ethics approval
Ethics application status

Summary
Brief summary
Trial website
Trial related presentations / publications
Public notes

Contacts
Principal investigator
Name 0 0
Novartis Pharmaceuticals
Address 0 0
Novartis Pharmaceuticals
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for public queries
Name 0 0
Address 0 0
Country 0 0
Phone 0 0
Fax 0 0
Email 0 0
Contact person for scientific queries

Data sharing statement
Will individual participant data (IPD) for this trial be available (including data dictionaries)?
Undecided
No/undecided IPD sharing reason/comment
Novartis is committed to sharing with qualified external researchers, access to patient-level data and supporting clinical documents from eligible studies. These requests are reviewed and approved by an independent review panel on the basis of scientific merit. All data provided is anonymized to respect the privacy of patients who have participated in the trial in line with applicable laws and regulations.

This trial data availability is according to the criteria and process described on www.clinicalstudydatarequest.com


What supporting documents are/will be available?

No Supporting Document Provided



Results publications and other study-related documents

No documents have been uploaded by study researchers.